Shortly after this publication, Bogdanove struck up a collaboration with Daniel Voytas, a plant geneticist at the University ...

Aaron Scott, of Fayetteville, is the first in North Carolina to receive a new FDA-approved therapy which uses the patient's own cells to relieve the pain of sickle cell disease.

BEAM-302 "has set the bar for efficacy in this space," William Blair analysts wrote in an investor note on Monday.

In the first part of his video interview with Pharma Commerce Editor Nicholas Saraceno, Jason C. Foster, CEO of Ori Biotech, offers his perspective on the state of CGTs, along with their potential for ...

The small study in patients with a rare disorder that causes liver and lung damage showed the potential for precisely ...

Prince Frederik of Luxembourg died from a genetic disease called PolG, but experts hope his passing could bring more ...

Dosing Initiated in Cohort 2 of the MyPEAK™-1 Phase 1b/2 Clinical Trial of TN-201 for Treatment of MYBPC3-Associated Hypertrophic ...

A single molecular switch is essential for blood stem cells to enter an activated, regenerative state in which they produce ...

Roche has recently launched a “fundamental reorganization” of Spark Therapeutics, the gene therapy unit that the Swiss pharma ...

Ms. Arakawa, the wife of the actor Gene Hackman, died from the effects of a disease often caused by contact with droppings ...

The tragic deaths of Gene Hackman and his wife Betty Arakawa have brought hantavirus into the spotlight – but what is it and ...

Beam Therapeutics said it used a form of CRISPR called base editing to correct, in several patients, a mutation that drives a ...