This is the first time such results have been achieved in both children and adult patients born with a specific type of ...

Neurogene Inc. (Nasdaq: NGNE), a clinical-stage company founded to bring life-changing genetic medicines to patients and ...

Gene therapy for sickle cell disease may help improve a major contributing factor to stroke risk in patients, reports a new ...

Researchers have developed a gene therapy that significantly slowed motor function loss in preclinical models of amyotrophic ...

The Alliance for Regenerative Medicine has voiced deep disappointment about reports that the FDA has put the director of its ...

The reported dismissal of high-ranking CBER officials Nicole Verdun and Rachael Anatol resurfaced lingering concerns about ...

“We now have emerging data to at least evaluate the efficacy of gene therapy in patients with a risk of or history of stroke,” Sharma said. “Until now, we only had one option that had a long-term ...

In the first part of this series, we explored how early genetic screening and gene therapy transform the lives of newborns and their families. Now, we’re taking an even earlier step: treating ...

Building blocks for flexible bioprocessing must also be easy to install and take little time to train operators.

DelveInsight's Frontotemporal Dementia Market Insights report includes a comprehensive understanding of current treatment ...