Vincent Gaynor remembers, almost to the minute, when he realized his part in birthing the breakthrough gene therapy Zolgensma ...
Recent research takes aim at the a variant in gene SCN1B, which causes a severe form of developmental epileptic encephalopathy.
This achievement follows Bahrain’s landmark decision on 2 December 2023 to become the second country globally and the first ...
A young man who was functionally blind is now able to read letters and words again after undergoing groundbreaking gene ...
GenSight Biologics announces efficacy and safety results for Lumevoq gene therapy at the conclusion of the REFLECT phase III clinical study: Paris Thursday, February 13, 2025, 17: ...
Dec. 10, 2024 — In a single IV injection, a gene therapy targeting cBIN1 can reverse the effects of heart failure and restore heart function in a large animal model. The therapy increases the ...
The Bahrain Oncology Centre (BOC) has made medical history by successfully treating a sickle cell disease (SCD) patient using ...
Irish Examiner on MSN7h
'For the first time in a decade, I can see': Gene therapy in Dublin restores blind man's sightSligo man can now see 'outlines and blobs of colours' after the groundbreaking ocular gene therapy surgery in the Mater Hospital ...
Pharmaceutical announced new data demonstrating treatment with UX111 AAV gene therapy led to a statistically significant ...
Rocket Pharmaceuticals, Inc.'s innovative therapies show promise after FDA setbacks. With potential $1B+ markets, RCKT offers ...
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