This is the first time such results have been achieved in both children and adult patients born with a specific type of ...

Neurogene Inc. (Nasdaq: NGNE), a clinical-stage company founded to bring life-changing genetic medicines to patients and ...

Gene therapy for sickle cell disease may help improve a major contributing factor to stroke risk in patients, reports a new study from St. Jude Children's Research Hospital. Many people with ...

Researchers have developed a gene therapy that significantly slowed motor function loss in preclinical models of amyotrophic lateral sclerosis (ALS ...

“We now have emerging data to at least evaluate the efficacy of gene therapy in patients with a risk of or history of stroke,” Sharma said. “Until now, we only had one option that had a long-term ...

Building blocks for flexible bioprocessing must also be easy to install and take little time to train operators.

June 27, 2025) Gene therapy for sickle cell disease may help improve a major contributing factor to stroke risk in patients, reports ...

DelveInsight's Frontotemporal Dementia Market Insights report includes a comprehensive understanding of current treatment ...

TECH teams up with USP to boost mAb and gene therapy testing, aiming to simplify analytics and enhance product quality.

A new gene therapy delivery device could let hospital pharmacies make personalized nanomedicines to order. This democratized ...

Last month, a baby got the world’s first personalized gene-editing treatment. What will this mean for millions of others with ...