The infant was born with a metabolic disorder called severe carbamoyl phosphate synthetase 1 (CPS1) deficiency, in which the ...

In a historic medical breakthrough, a child diagnosed with a rare genetic disorder has been successfully treated with a ...

Awakening's Arrakis are moisture seals: puffy wads of fabric that fill cave entrances to create makeshift microclimates, ...

Treated with an individualized gene-editing therapy that corrects mutations directly on the genome, a patient shows ...

The miracle of this penultimate episode of Andor is that despite knowing how everything turns out for just about everyone left on the show — their futures are spelled out in the prequel film Rogue One ...

A newborn boy, KJ, was diagnosed at birth with a rare and potentially fatal genetic disease. He received a novel, on-demand CRISPR therapy in record time.

Since the development of CRISPR gene editing, leaders in the field have foreseen a future in which CRISPR could be used to repair any genetic disease ? including rare "N-of-1" diseases caused by ...

Expedition 33 can make a great build even better. The RPG title by Sandfall Interactive is not an easy game, especially on the Expeditioner difficulty.

Nicklas, MD, PhD, and Penn Medicine's Kiran Musunuru, MD, PhD. Credit: CHOPPHILADELPHIA & NEW ORLEANS – In a historic medical ...