INDIANAPOLIS (WISH) — It’s a devastating diagnosis that changes a child’s life forever, Duchenne muscular dystrophy, or DMD, is a rare and fatal genetic disease that primarily affects boys. It slowly ...

Fresno firefighters are taking action and asking for your help. Monday morning, firefighters will be in north Fresno asking ...

Participating partners include, Alaska Commercial Company, Albertsons Companies Foundation, American Furniture Warehouse, ...

Despite recent challenges ranging from wildfires to economic uncertainty, Los Angeles remains a prime destination, not only ...

Panelists discuss how spinal muscular atrophy (SMA) progresses over time, affecting motor function differently in older ...

The therapy used molecules called antisense oligonucleotides, or ASOs, that can alter the expression of genes through interactions with RNA, which creates proteins. ASOs are currently given to babies ...

Scientists present current evidence for a new gene therapy for Duchenne muscular dystrophy called delandistrogene moxeparvovec.

To help neurologists, clinicians and families understand the current evidence for a new gene therapy for Duchenne muscular ...

Delandistrogene moxeparvovec (Elevidys; Sarepta Therapeutics) appeared to protect muscle from progressive damage in patients ...

Hopkins neuroscientist Richard Huganir is close to finding a potential life-changing treatment for kids with SYNGAP1-related ...

Winnacunnet High School senior Joe Labrecque has transformed his battle with a rare chronic illness into a mission to help ...

Dyne Therapeutics, Inc.’s DYN share price has dipped by 7.11%, which has investors questioning if this is right time to buy.