Apr. 28, 2025 — To help achieve more precise control of gene therapy, engineers have designed a new control circuit that can keep gene expression levels within a target range. The method could ...

A boy with an ultra-rare immune disease which can carry a “death sentence” is living a normal life after taking part in a groundbreaking gene therapy trial. Four-year-old Eisa Hussain now ...

He added: “Great Ormond Street told us they couldn’t find a bone marrow match so they offered the gene therapy, I said ‘if that’s the only option they have, we have to do it’.

A new gene therapy developed at the Children's Hospital of Philadelphia has been approved by the FDA and is being used to transform lives. The first patient to receive this gene therapy after it ...

April 29 (Reuters) - The U.S. Food and Drug Administration approved Abeona Therapeutics' (ABEO.O), opens new tab gene therapy for a rare skin disorder on Tuesday. The gene therapy, called Zevaskyn ...

A boy with an ultra-rare immune disease which can carry a “death sentence” is living a normal life after taking part in a groundbreaking gene therapy trial. Four-year-old Eisa Hussain now enjoys ...

Persistence has paid off for Abeona Therapeutics and its gene therapy for recessive dystrophic epidermolysis bullosa (RDEB). About a year after the FDA rejected the company's prior approval filing ...

VERVE-102, developed by Verve Therapeutics, is a cutting-edge CRISPR base editing therapy. Unlike traditional gene editing that cuts DNA, base editing makes a tiny, precise change: it switches off ...

The β 2 common integrin subunit CD18 is essential for leukocyte–endothelial adhesion and extravasation to inflamed or infected tissue. Damaging variants in ITGB2, which encodes CD18, cause ...