Nanoscope Therapeutics is on the brink of filing for FDA approval of what could be the first gene therapy for incurable eye disease retinitis pigmentosa (RP) that can be used regardless of ...

The gene therapy launched in the US last year with a $3.5 million price tag as a one-time therapy for adults with moderate to severe haemophilia B who need factor IX (FIX) replacement therapy, but ...

Genes and Genetics News. Read today's medical research in genetics including what can damage genes, what can protect them, and more.

CRISPR-Cas9 genome editing articles from across Nature Portfolio. Atom; RSS Feed; Definition. CRISPR-Cas9 genome editing exploits the CRISPR-Cas system to modify a genome in a targeted manner.