News

Cancer can be made worse by high-dose radiotherapy, surprising new study finds
Findings of University of Chicago cancer centre research led by China-born biochemist Yang Kaiting have been published in ...
Smithsonian Magazine16h
In a Remarkable First, a Baby With a Rare Disease Receives Personalized Gene Therapy
Researchers say the CRISPR-based technique used could eventually be employed to treat more people with rare genetic diseases ...
Scientists Edited Genes Inside a Living Person for the First Time—and Saved His Life
With grim prognosis hanging overhead, doctors and scientists at universities and institutions across the U.S. worked ...
STAT23h
When the FDA requires a large vaccine trial, who pays?
In the Phase 2 study of patients with chronic kidney disease, the highest dose of the drug lowered by 86% the levels of ...
Opinion
An Anti-Science MAHA Extremist Is Playing a Major Role at the FDA
On first glance, Dr. Vinay Prasad’s medical credentials sound impressive. But look closer and you’ll find a narcissistic attention-seeker peddling misinformation, whose views will cost lives.
Nature2d
World first: ultra-powerful CRISPR treatment trialled in a person
The only gene-editing therapy currently on the market is a CRISPR–Cas9-based treatment for two blood disorders, sickle-cell ...
Doctors Achieve Medical Breakthrough Using Gene-Editing Therapy to Heal Baby with Rare Disorder
Doctors have successfully used gene-editing therapy to treat an infant born with a rare disorder. Experts believe the ...
Public Broadcasting Service (PBS)4d
Breakthrough gene editing treatment helps child born with rare disorder
Doctors announced this week that they have treated a newborn baby with a rare genetic disease using the world’s first personalized gene editing therapy. Geoff Bennett discussed the treatment and its ...
STAT4d
Day 3 at ASGCT: Vinay Prasad speculation, screening newborns, promising data
A hot (if cautious) topic at the big gene therapy meeting: what Vinay Prasad's appointment might mean for approvals in rare ...
Healio4d
Infant with rare disease receives world’s first personalized gene-editing therapy
An infant with a rare urea cycle disorder became the first patient to receive a personalized gene-editing therapy. His care ...
How an experimental gene editing treatment helped a desperately ill baby
The baby KJ Muldoon suffers of a rare genetic disease, but now thanks to an experimental gene editing treatment, he is now on ...
Doctors save baby's life with first-ever gene fix for deadly rare disease
The goal is to reuse key parts of the treatment and simply swap in a custom set of instructions for each patient's specific gene mutation, doctors say.