Experts make case for early testing, prevention and careIn this report, VINCENT KURAUN explores the groundbreaking strategies for managing sickle cell disease, with a particular focus on crisis ...

The agency narrowed who can get the shot and added new study requirements that could cost the company tens of millions.

Doctors have successfully used gene-editing therapy to treat an infant born with a rare disorder. Experts believe the ...

A baby with CPS1 is thriving after receiving the first personalized gene therapy for the condition, offering new hope to ...

The baby KJ Muldoon suffers of a rare genetic disease, but now thanks to an experimental gene editing treatment, he is now on ...

The signs of diabetes in kids include increased thirst, frequent urination, and irritability. Learn more signs and when to ...

PHILADELPHIA (WPVI) -- An infant, who was born with a deadly disease, is now thriving, thanks to a medical first performed at ...

The goal is to reuse key parts of the treatment and simply swap in a custom set of instructions for each patient's specific gene mutation, doctors say.

Olivia Fox was diagnosed with a brain tumor on her 1st birthday and is undergoing targeted chemo doctors hope will help her ...

Corey and Diana Sullivan are reunited with their three children after a 19-month custody battle which began when they took ...

House Bill 544 marks a transformative step in ensuring access to vital prescription drugs, specifically biologics for people ...