Spinal muscular atrophy, or SMA, is a genetic neurodegenerative disorder that about one in every 6,000 babies are born with, ...

My favorite story as a 38-year-old man living with Spinal Muscular Atrophy Type II, a form of Muscular Dystrophy that renders ...

I had the pleasure of attending a Netflix event around the WoW documentary The Remarkable Life of Ibelin last year—one that ...

The Supreme Court summons five social media influencers, including Samay Raina, over allegations of mocking individuals with ...

In which young patients with spinal muscular atrophy will spinal braces and growing rods be most helpful? Ashley Webb, MD, assistant professor of pediatric neurology and neuromuscular program ...

A generic version of Risdiplam, a medicine used to treat spinal muscular atrophy (SMA), could soon be available in India at $183.47 dollars per bottle, a sharp 97% drop from the current rate of $ ...

(0:54) How does one time surgery for scoliosis in children with pediatric spinal muscular atrophy get a maximum benefit without impeding growth? Dr. Ashley E. Webb of the University of Texas ...

Despite significant advancements in spinal muscular atrophy (SMA) management, unmet needs persist, especially for patients aged 2 and older without early treatment. Spinal muscular atrophy (SMA ...

Ross Lannon shared the footage in an effort to highlight how "simple decisions can have a big impact on others." ...

Nevada two years ago began using American Rescue Plan Act dollars to expand screenings of newborns for rare diseases. With ...