Spinal muscular atrophy, or SMA, is a genetic neurodegenerative disorder that about one in every 6,000 babies are born with, ...

I had the pleasure of attending a Netflix event around the WoW documentary The Remarkable Life of Ibelin last year—one that ...

An application was was recently filed by M/s Cure SMA Foundation[1] against the controversial comedian Samay Raina with ...

Learn more about whether BioCryst Pharmaceuticals, Inc. or PTC Therapeutics, Inc. is a better investment based on AAII's A+ Investor grades, which compare both companies' key financial metrics.

The administration has approved 120 billion rials (some 144,000 dollars) for treating rare and hard-to-treat diseases in the ...

The Timbermills.” In theory, Jimmy is Francis’ designated companion in one of two wheelchair accessible areas at ground level ...

Digital PCR to simultaneously detect SMN1 gene defects and the number of SMN2 copies to diagnose SMA matches standard methods ...