News

Eton Pharmaceuticals Set To Dominate Orphan Drug Niche
Eton Pharmaceuticals is able to buy orphan drugs from large pharma companies, where they are too small to matter. Read why ...
US FDA Orphan Drug Rare Disease Market Clinical Trials Drug Sales Insight 2030
Kuick Research Report Gives Detailed Insight On More Than 1400 FDA Orphan Designated Drugs And Highlights More Than USD 190 ...
News-Medical.Net on MSN6d
EMA designates allopurinol as first orphan drug for the treatment of Marfan syndrome
The European Medicines Agency (EMA) has designated allopurinol as the first orphan drug for the treatment of Marfan syndrome, ...
Allopurinol designated as the first orphan drug for Marfan syndrome treatment
The European Medicines Agency (EMA) has designated allopurinol as the first orphan drug for the treatment of Marfan syndrome, a rare connective tissue disease which has no cure to date. This disease ...
Prices for new US drugs doubled in 4 years as focus on rare disease grows
U.S. President Donald Trump's trade negotiators are pushing the EU to make unilateral tariff reductions on U.S. goods, saying ...
CNS Pharmaceuticals Acquires Orphan Drug Designation for Novel, Late Stage Abeotaxane, TPI 287
Company advancing plans to develop TPI 287, a novel, late stage abeotaxane that appears to cross the blood-brain barrier and ...
Quoin Pharmaceuticals Announces European Medicines Agency (EMA) Grants Orphan Drug Designation for QRX003 for the Treatment of Netherton Syndrome
Company continues to advance QRX003 in late-stage clinical trials in Netherton Syndrome patients Regulatory milestone ...
Mirage News6d
Allopurinol: First Orphan Drug for Marfan Syndrome
The European Medicines Agency (EMA) has designated allopurinol as the first orphan drug for the treatment of Marfan syndrome, ...
PharmaTimes11d
Kaerus Bioscience secures orphan drug designation for fragile x syndrome treatment
Kaerus Bioscience has received orphan drug and rare paediatric drug designations from the FDA for KER-0193, its lead ...
Healio5d
FDA nudges development of drug to prevent necrotizing enterocolitis
The FDA recently granted orphan drug and rare pediatric disease designations to Infinant Health for a live biotherapeutic ...
News Medical7d
EMA designates allopurinol as first orphan drug for the treatment of Marfan syndrome
The European Medicines Agency (EMA) has designated allopurinol as the first orphan drug for the treatment of Marfan syndrome, a rare connective tissue disease which as no cure to date. This ...