The ASO for myotonic dystrophy type 1 was well tolerated and improved splicing and function in a study presented at ASGCT.

QurAlis' FlexASO® platform was developed to generate splice-switching ASOs with improved potency, increased therapeutic index and improved bio-distribution. This bespoke platform has the potential to ...

The interaction between RNA-binding proteins (RBPs) and circular RNAs (circRNAs) has emerged as a key area of interest in ...

The interaction between RNA-binding proteins (RBPs) and circular RNAs (circRNAs) has emerged as a key area of interest in understanding cancer biology.

CircRNAs are unique RNA molecules formed through a back-splicing mechanism that connects the 5' and 3' ends of precursor mRNA ...

Cancer immunotherapy represents a transformative approach in oncology, especially for treating cancers thought to be incurable. However, a significant ...

An elegant screening strategy unveils a molecular actor that connects widespread changes in mRNA processing with a nutrient-sensing protein modification.

PTC Therapeutics Inc. CEO Matthew Klein said the firm “achieved all we set out to [achieve] in phase II” with PTC-518 in ...

The latest price target for Moderna (NASDAQ:MRNA) was reported by UBS on May 2, 2025. The analyst firm set a price target for $70.00 expecting MRNA to rise to within 12 months (a possible 174.91% ...

Moderna is currently in the very early stages of testing a bird flu vaccine using the same mRNA technology that allowed for rapid development and rollout of COVID-19 vaccines. The funds from the U.S.