Subtle changes in the brain, detectable through advanced imaging, blood and spinal fluid analysis, happen approximately 20 ...
Huntington's disease is a hereditary disorder caused by a genetic mutation in the HTT gene, leading to progressive brain cell ...
Beta blockers were associated with later appearance of motor symptoms and slower symptom worsening, but an outside expert ...
The oversubscribed Series B will boost the clinical development of two RNAi therapies for epilepsy and Huntington’s disease ...
A recent study published in Cell reveals that the repeated DNA sequence that leads to Huntington’s disease (HD) expands ...
The startup says its specially constructed RNAi therapies can get deep into brain tissue, yielding new ways to treat ...
Researchers have made a major breakthrough in our understanding of Huntington's disease. This genetic disorder has long been ...
Subtle changes in the brain, detectable through advanced imaging, blood and spinal fluid analysis, happen approximately twenty years before a clinical motor diagnosis in people with Huntington's ...
Huntington's disease, a fatal hereditary brain disorder, is linked to a genetic mutation that remains harmless for decades before expanding and producing toxic proteins that kill brain cells.
The company, co-founded by Nobel Laureate Craig Mello, aims to push molecules for Huntington’s and a form of epilepsy into ...