BioCryst has also filed its line extension application for the use of ORLADEYO oral granules in patients with HAE aged 2 to 11 years with the European Medicines Agency. Additional regulatory filings ...

Ari Aster’s debut feature Hereditary brings forth those murky questions. Perhaps, in the end, it’s all the same kettle of demons, but there’s something to Aster’s approach that seems to ...

Having a close relative, such as a parent, sibling, or grandparent, who has high levels of cholesterol is called familial hypercholesterolemia, and it means you may be at a higher risk of having ...

Background: In this study we included patients with hereditary angioedema (HAE) caused by decreased levels of C1 inhibitor (HAE-C1INH). An increased risk of autoimmune disorders, particularly systemic ...

Stroke/abscess risk factors have not been defined. Methods: A cohort study of 323 consecutive individuals with PAVMs (n = 219) and/or the commonly associated condition hereditary haemorrhagic ...

We investigated the presence and cellular localisation of hepcidin in the liver and developed a non-invasive assay to analyse its regulation in patients with hereditary haemochromatosis (HH), chronic ...

Breast cancer is the most common cancer in women in the United States, except for skin cancers. It accounts for about 30% (or 1 in 3) of all new female cancers each year. The American Cancer Society's ...

The company is on track to complete enrollment in the global Phase 3 HAELO study for hereditary angioedema (HAE) by the third quarter of 2025 and has dosed the first patient in the Phase 3 ...

15 million followers, Rs 266 crore in a day: Why this couple is quitting live-streaming. In a significant development that has drawn widespread attention, a Chinese couple with 15 million ...

The US Food and Drug Administation (FDA) has approved BlackfinBio Limited’s Phase 1/2 clinical trial for its novel adeno-associated virus (AAV) gene therapy targeting Hereditary Spastic Paraplegia ...

ncl.ac.uk Leber hereditary optic neuropathy (LHON) is a mitochondrial genetic disease that preferentially causes blindness in young adult males, affecting about 1 in 25 000 of the British population.