A new nasal spray-based gene therapy, using AAV.CPP.16 shows promise for treating lung diseases like COVID-19 and pulmonary ...

FLT201 showed durable response and superior reduction of disease-causing substrate compared to ERT, underscoring its potential to improve upon standard of careLONDON, May 27, 2025 (GLOBE NEWSWIRE) -- ...

A patient has died in a pivotal Phase II trial of Rocket Pharmaceuticals’ gene therapy for Danon disease after suffering a ...

Wilson's new company, Philadelphia-based Gemma Biotherapeutics, plans to start testing gene therapies in Brazil this year.

Researchers have developed a new viral delivery system designed efficiently to target the lungs and respiratory airways. It could help in tackling various respiratory illnesses including pulmonary fib ...

Broad Institute researchers have developed a way to edit the genetic sequences at the root of Huntington's disease and ...

Genetic defects are exceedingly common, which is not surprising considering just how many cells make up our bodies, including our reproductive cells. While most of these defects have no or only ...

Enanta Pharmaceuticals, Inc. , a clinical-stage biotechnology company dedicated to creating small molecule drugs for viral infections and immunological diseases, today announced that Jay R. Luly, Ph.D ...

Candel Therapeutics essentially uses a dual-virus strategy with CAN-2409 and CAN-3110 immunotherapies. Find out why CADL ...

Latus Bio, Inc. has announced a significant advancement in the field of gene therapy with the publication of its latest ...

"These deaths are driven by long-running crises in drug overdose, gun violence, car collisions, and preventable cardiometabolic deaths," said coauthor Elizabeth Wrigley-Field, PhD. Other news is on ...