Findings of University of Chicago cancer centre research led by China-born biochemist Yang Kaiting have been published in ...

Researchers say the CRISPR-based technique used could eventually be employed to treat more people with rare genetic diseases ...

With grim prognosis hanging overhead, doctors and scientists at universities and institutions across the U.S. worked ...

In the Phase 2 study of patients with chronic kidney disease, the highest dose of the drug lowered by 86% the levels of ...

Doctors have successfully used gene-editing therapy to treat an infant born with a rare disorder. Experts believe the ...

Doctors announced this week that they have treated a newborn baby with a rare genetic disease using the world’s first personalized gene editing therapy. Geoff Bennett discussed the treatment and its ...

An infant with a rare urea cycle disorder became the first patient to receive a personalized gene-editing therapy. His care ...

KJ Muldoon became the first patient to undergo personalized CRISPR treatment, a therapy that found the one uniquely mutated gene out of 20,000 in his little body, and fixed it.

The goal is to reuse key parts of the treatment and simply swap in a custom set of instructions for each patient's specific gene mutation, doctors say.

KJ Muldoon was born with a devastating medical problem. Racing to solve it, doctors may have launched a 'road map' for a new type of treatment.

Treated with an individualized gene-editing therapy that corrects mutations directly on the genome, a patient shows ...

A range of other rare inherited diseases are now likely to be curable by similar procedures, the research team said ...