That leads to a buildup of ammonia that destroys the liver and can cause neurological damage with lifelong consequences. His ...

A recent report from the St James Health Department has brought renewed attention to the troubling reality of rodent ...

Scientists sprinted to create personalized medicine for baby KJ powered by CRISPR, a powerful gene-editing technology that ...

An infant with a rare urea cycle disorder became the first patient to receive a personalized gene-editing therapy. His care ...

A Delaware County infant with a rare metabolic disease, CPS1 deficiency, was treated at CHOP with a custom CRISPR therapy.

Urea, ammonia exporter eyes growth via cost cuts ... a 7% increase in own-produced volumes versus Q1 2024 and a strong safety record. The company also launched a new $35 million cost-saving ...

In a medical first that could revolutionize treatment for thousands of rare genetic diseases, doctors have successfully used ...

A blood test revealed toxic levels of ammonia building up in KJ’s body, threatening to damage his brain — a sign of an ultrarare ... vet its safety and use it to fix an errant gene making ...

Acwa Power has signed Memorandums of Understanding (MoUs) worth $500 million with US companies, building on its existing ...

KJ received the first dose through an infusion in February, followed by two additional doses in March and April. Doctors ...