Deadly motor-neuron disease treated in the womb in world 1st
An infant with a fatal genetic disease has survived past the age of 2 with no signs of the condition, thanks to treatment ...
Neurona Unveils Phase 3 EPIC Study for NRTX-1001 Cell Therapy in Epilepsy
Based on alignment gained with FDA under the Regenerative Medicine Advanced Therapy (RMAT) designation, Neurona plans to conduct the Phase 3 ...
Promising results from first prenatal therapy for spinal muscular atrophy
Spinal muscular atrophy (SMA) is a progressive neurodegenerative disorder set in motion before birth. Scientists at St. Jude ...
News Medical4d
Human organoids for AAV capsid selection
Organoids were cultured from healthy donor iPSC sources and differentiated using the human iPSC-derived Cerebral Organoid ...
EurekAlert!5d
SwRI collaborates with UTSA to track neurons with machine vision algorithms
A team led by Southwest Research Institute (SwRI) developed a computational method to improve techniques to track brain cell development over time. By studying neurons and their dynamics in brain ...
Zebrafish study uncovers spatial cues that shape neuron diversity beyond gene expression
Max Planck Institute for Biological Intelligence researchers have identified over 60 transcriptomic neuron types in the ...
MIT Technology Review9d
Motor neuron diseases took their voices. AI is bringing them back.
AI-generated voice clones are bringing back the voices of people with MND, allowing some to communicate, connect, and even ...
The American Journal of Managed Care10d
Risdiplam Tablet for Spinal Muscular Atrophy Receives FDA Approval
The 5 mg risdiplam tablet provides the same efficacy and safety for spinal muscular atrophy as the currently available oral ...