Pepgen will stop development of its Duchenne MD exon-skipping therapy PGN-ED051 after increases in dystrophin levels proved ...

With FSHD, the need to adapt seems never-ending, which is why columnist Robin Stemple and others feel like they're constantly ...

CureDuchenne is investing $1 million in Entos Pharmaceuticals to support the development of a new DMD gene therapy.

DMD treatment SAT-3247 was safe and well-tolerated, and showed signs of increasing muscle strength in five adults, Satellos ...

Columnist Shalom Lim stood up for his right to inclusive access to a major sporting event — and a local soccer club responded ...

Long-term data from Genethon’s GNT0004 Phase 1/2 trial reveal sustained motor function in boys with Duchenne muscular ...

A number of strategies can help to ensure adequate joint care to best manage joint pain and stiffness in Duchenne muscular ...

New data demonstrated the benefits of Elevidys, a gene therapy for multiple Duchenne muscular dystrophy, in different age ...

After taking a day for reflection on her sons' lives with DMD, columnist Betty Vertin says she feels more on top of their care.

A couple of speeches recently helped columnist Betty Vertin newly appreciate how much motherhood has been her life purpose.