Liver damage related to Zolgensma gene therapy usually resolves within a few months of treatment, a study found.

Nothing could've prepared columnist Helen Baldwin for her late son Jeffrey's diagnosis of SMA type 1 in the late 1990s.

In her debut column of "Caring Together," Connie Chandler reflects on her college days, when friends volunteered to help with ...

Connie Chandler is the director of family engagement at the nonprofit organization We Carry Kevan. She grew up in the ...

For a boy with SMA in China, starting Evrysdi (risdiplam) just 12 days after birth was safe and helped him reach key motor ...

Connie Chandler is a columnist for BioNews and the Director of Family Engagement at the nonprofit organization, We Carry Kevan. She grew up in the foothills of North Carolina but now owns a home and ...

Columnist Alyssa Silva's medical charts aren't a complete reflection of who she is. That's why she's defining health on her ...

Certain people and things provide the stability that columnist Ari Anderson needs to adjust to changes in his life with SMA.

Motor improvements in SMA adults treated with Spinraza paralleled a boost in electrical impulses along nerves that supply ...

Testing SMA patient DNA with advanced methods like HapSMA can reveal genetic changes that affect how severe the disease is, ...

Researchers studied 118 SMA type 2 patients and saw their RULM scores stayed higher than expected had their disease kept its ...