Gene therapy for sickle cell disease may help improve a major contributing factor to stroke risk in patients, reports a new ...

A research team at the University of Osaka has unveiled the molecular mechanism behind genome ejection from adeno-associated ...

“We now have emerging data to at least evaluate the efficacy of gene therapy in patients with a risk of or history of stroke,” Sharma said. “Until now, we only had one option that had a long-term ...

Gene therapy for blood stem cells has historically been challenging, expensive, and intrusive. Traditionally, it involved harvesting stem cells from a patient or donor, ...

With grim prognosis hanging overhead, doctors and scientists at universities and institutions across the U.S. worked tirelessly to develop the world’s first custom gene-editing therapy to save the ...

I n the 1990s, Lee Sweeney, a physiologist at the University of Pennsylvania, demonstrated that inserting the gene encoding insulin-like growth factor 1 (IGF-1) into the muscle cells of mice increased ...

News broke yesterday that researchers in Philadelphia appear to have successfully treated a 6-month-old baby boy, called KJ, with a personalized CRISPR gene-editing therapy.The treatment corrects ...

SEVILLE, Spain — Gene therapy is an area of intensive research and development in the retina space, with promising prospects and significant challenges. The benefits and pitfalls of gene therapy ...

RNA editing, then, is also a type of gene therapy. Its goal is to change how RNA interprets genetic instructions to control how proteins are made. In most recent advancements, ...

Three-year-old Gunreet Kaur has a rare inherited condition that affects children’s physical, mental and behavioural ...