Intrathecal treatment with a vector-based gene therapy was associated with a greater improvement in motor function at 52 ...
Clinical Trials Arena on MSN5d
Epicrispr secures $68m for facioscapulohumeral muscular dystrophy therapy trialEpicrispr Biotechnologies has raised $68m in the initial close of its Series B financing round to commence the clinical trial ...
Speakers from the Muscular Dystrophy Association (MDA) highlighted 75 years of progress in understanding and treating ...
Muscular Dystrophy Association and Burn Boot Camp Team Up for the 9th Annual 'Be Their Muscle' Philanthropic Event ...
The FDA has approved Evrysdi in tablet form for patients with spinal muscular atrophy aged 2 years ... for ALS was linked to a slowing of disease-progression milestones compared with no IV ...
Neuromuscular diseases encompass a wide range of disorders characterized by progressive muscle weakness and dysfunction, resulting from abnormalities in the ...
New research led by the University of Portsmouth has revealed how Duchenne muscular dystrophy (DMD), best known for causing ...
The startup is using CRISPR tools to stop errant expression of a gene linked to facioscapulohumeral muscular dystrophy, a ...
New Discovery Enables Gene Therapy for Muscular Dystrophies, Other Disorders Nov. 14, 2024 — StitchR, a new gene therapy technique, delivers large genes in two parts to treat muscular ...
News Medical on MSN5d
University of Houston pharmacy team discovers target to repair injured musclesA team at the University of Houston College of Pharmacy has discovered a possible therapeutic approach to repair injured ...
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