He had a hunch that the oral SMA treatment risdiplam, made by Roche, had prenatal potential because it’s safe for kids and ...

In which young patients with spinal muscular atrophy will spinal braces and growing rods be most helpful? Ashley Webb, MD, assistant professor of pediatric neurology and neuromuscular program ...

Public health activists estimate Roche earned significantly more from risdiplam, a spinal muscular atrophy drug, than its ...

Despite significant advancements in spinal muscular atrophy (SMA) management, unmet needs persist, especially for patients aged 2 and older without early treatment. Spinal muscular atrophy (SMA ...

The evolution of functional assessments for spinal muscular atrophy (SMA) highlights the challenges of adapting pediatric scales for adults and the need for modified evaluations to accurately ...

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The Supreme Court summons five social media influencers, including Samay Raina, over allegations of mocking individuals with ...

Showing his big heart and the immense affection he has for Mexicans, American singer Drake Bell visits a Mexican child in the ...

How does one time surgery for scoliosis in children with pediatric spinal muscular atrophy get a maximum benefit without impeding growth? Dr. Ashley E. Webb of the University of Texas Health ...

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